News

Bay Area family shares frustrations after FDA rejects drug for ultra-rare Barth Syndrome
With the FDA recently rejecting a drug application that aims to help those living with Barth Syndrome, one Bay Area family is ...
First oral drug shows promise for Barth syndrome heart and muscle symptoms
Researchers at Tohoku University have discovered that an oral drug called MA-5 can improve both heart and muscle problems in ...
News Medical on MSN3d
Oral Drug Promising for Barth Syndrome Symptoms
Researchers at Tohoku University have discovered that an oral drug called MA-5 can improve both heart and muscle problems in ...
Bay Area family affected by Barth Syndrome frustrated by delay of approved treatments
With the FDA recently rejecting a drug application that aims to help those living with Barth Syndrome, one Bay Area family is ...
EurekAlert!3d
First oral drug shows promise for Barth syndrome heart and muscle symptoms - EurekAlert!
Barth syndrome is a rare genetic disorder with no known cure. Researchers at Tohoku University examined a new oral drug called MA-5 that could provide life-changing relief to these young patients.
Channel 30006d
Family shares frustrations after FDA rejects drug for ultra-rare Barth Syndrome - Channel 3000
It's the only drug for Barth Syndrome clinical trials. After several delays, however, the FDA announced it will not be approving the drug application.