Amyloid transthyretin cardiomyopathy (ATTR-CM) is a progressive and life-threatening heart disease that can lead to increased ventricular wall thickness, restrictive cardiomyopathy, and heart failure.

A risk of pregnancy complications and adverse birth outcomes has been observed in mothers with alpha-1 antitrypsin deficiency (AATD), according to a study recently published in Plos One. The ...

Which of the statements below about the complications of immunoglobulin G4-related disease (IgG4-RD) are correct? Select one of the options for each question, then submit your answers to see how well ...

After some stumbles out of the gate, an experimental treatment that’s part of a group hoping to be the next big thing for people with multiple sclerosis (MS) is a step closer to US Food and Drug ...

For patients with eosinophilic granulomatosis with polyangiitis (EGPA)—a type of antineutrophil cytoplasmic antibody (ANCA)-associated vasculitis (AAV) that is mediated largely by ...

Diffuse large B-cell lymphoma (DLBCL) is a type of cancer that originates in and affects the lymphatic system. 1 It is the most common type of non-Hodgkin lymphoma (NHL), accounting for approximately ...

The CSHA Clinical Frailty Scale (CFS) is a valuable tool for predicting treatment-related toxicity and discontinuation in older adults receiving targeted therapy for chronic lymphocytic leukemia (CLL) ...

A recent study highlighted the significant burden of indolent systemic mastocytosis (SM) and offered a framework for comparing diseases and informing healthcare priorities. The findings estimated the ...

The administration of ARGX-119 led to improved survival and muscle function in a passive transfer myasthenia gravis (MG) mice model; however, the efficacy appears to be limited to a subset of patients ...

A strong association has been observed among patients with systemic mastocytosis (SM) who harbor the somatic missense KIT p.D816V variant in peripheral blood leukocytes and severe sting anaphylaxis. A ...

A male patient initially suspected of having immunoglobulin G4-related disease (IgG4-RD) had his diagnosis revised to Castleman disease following further investigations. This case report was published ...

Treatment with risdiplam over 30 months led to overall clinically meaningful improvement in most adult patients with spinal muscular atrophy (SMA) type 2 or 3, according to a single-center ...