Spinal muscular atrophy affects all the body's muscles. For a long time, it was considered a disease caused solely by the ...

Emma, a third-grader with big plans for her future, received a groundbreaking treatment at just the right time.

Spinal muscular atrophy with respiratory distress (SMARD) is a rare genetic condition that typically affects infants and children. It causes muscle weakness and breathing problems. Spinal muscular ...

The first prenatal treatment for spinal muscular atrophy showed promise in a single case report. Risdiplam was given to the mother during pregnancy and to the child after birth. More than 2 years ...

An orally administered drug to redistribute excess iron and lower cellular oxidative stress was found to slow disease ...

After menopause, women with MS show accelerated loss of volume in brain structures associated with memory, attention, and problem-solving.

Scientists report results from a promising new approach to treat the rare neurodegenerative disorder. Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before ...

Lundbeck to showcase amlenetug Phase 3 MASCOT trial design in Multiple System Atrophy at the International Congress of Parkinson’s Disease and Movement Disorders® 2025·     Details of the Phase 3 ...

Animals that hibernate are incredibly resilient. They can spend months without food or water, muscles refusing to atrophy, body temperature dropping to near freezing as their metabolism and brain ...